CPLANE1

Clinical Characteristics

Joubert syndrome (JBTS) is a ciliopathy, and the related gene encodes primary cilia proteins with important roles in the development of many organs, with variants causing mid-hindbrain malformation. JBTS is characterized by developmental delay, hypotonia, abnormal breathing patterns, oculomotor apraxia, and a specific brain malformation on brain MRI: the “molar tooth sign.”