EFNB1

Clinical Characteristics

Classic presentation occurs in affected females with widely spaced eyes, a grooved nasal tip and unilateral or bilateral coronal suture premature fusion.
As well as some variable but frequent manifestations, such as frizzy hair, cleft lip and/or palate, congenital elevation of shoulder blade (Sprengel anomaly), webbing of fingers and toes and longitudinal ridging of the nails.
Therefore, some extracranial defects have been described too, such as cardiac, abdominal and genitourinary anomalies.


Next, we present with a clinical synopsis of the clinical features:

Females:
Head
•    Short and broad skull (Brachycephaly)

Face
•    Frontal bossing
•    Facial asymmetry
•    Widow’s peak

Eyes
•    Hypertelorism
•    Telecanthys
•    Exotropia
•    Nystagmus
•    Strabismus
•    Downslanting palpebral fissures
•    Ocular melanosis

Nose
•    Bifid nasal tip
•    Hypoplastic nasal tip

Mouth
•    Cleft lip
•    Cleft palate

Neck
•    Short neck

Chest
•    Narrow sloping shoulders
•    Congenital elevation of shoulder blade (Sprengel deformity)
•    Pectus excavatum
•    Unilateral breast hypoplasia

Heart
•    Atrial septal defect
•    Bicuspid aortic valve
•    Ventricular septal defect
•    Hypertrophic cardiomyopathy
•    Wolff-Parkinson-White syndrome

Abdomen
•    Umbilical hernia
•    Congenital diaphragmatic hernia

Genitourinary
•    Uterus didephys
•    Duplex kidney
•    Septate vagina

Skull
•    Coronal craniosynostosis (uni or bilateral)

Limbs
•    Asymmetric lower limb shortness
•    Joint laxity

Hands
•    Webbing fingers (Syndactyly)
•    Short fingers (Brachydatyly)
•    Fifth finger clinodactyly

Feet
•    Syndactyly
•    Broad halluces

Skin
•    Axillary pterygia

Nails
•    Brittle nails
•    Longitudinal splitting
•    Grooved nails

Hair
•    Thick, wiry hair
•    Widow’s peak
•    Low posterior hairline

Neurologic
•    Developmental delay
•    Floppy infant (Hypotonia)
•    Hypoplasia or agenesis of corpus callosum

Males present with a less severe phenotype, sometimes showing only mild clinical features such as hypertelorism or some others, with congenital diaphragmatic hernia, but without other distinctive anomalies, as in females.

Carrier males (might present with only one of the features):
•    Mild clinical features

Height
•    Short stature

Head
•    Brachycephaly
•    Frontal bossing
•    Thick, wiry hair

Face
•    Hypertelorism

Hands
•    Brachydactyly

Abdomen
•    Congenital diaphragmatic hernia

Genitourinary
•    Hypospadias
•    Shawl scrotum
•    Undescended testicle (Cryptorchidism)