PSMC3

Professionals

Variants in PSMC3 cause an autosomal dominant disorder characterized mainly by neurodevelopmental impairment (delayed or impaired speech, intellectual disability, abnormal behavior, hypotonia), dysmorphic facial features and congenital malformations (skeletal, cardiac,). The disorder is rare, with a prevalence difficult to estimate exactly, but the princeps study identified more than 20 affected individuals.