SMAD3

Clinical Characteristics

Patients mostly present with these features:

  • Aortic root aneurysm and dissection
  • Aortic/arterial aneurysm and dissection (widespread and aggressive)
  • Arterial tortuosity (most prominently head and neck vessel)
  • Osteoarthritis
  • Pectus deformity
  • Scoliosis
  • Cervical spine instability
  • Spondylolisthesis
  • Joint laxity
  • Arachnodactyly
  • Camptodactyly
  • Club foot
  • Pes planus
  • Bifid uvula
  • Cleft palate
  • Retrognathia
  • Hypertelorism
  • Soft and velvety skin
  • Translucent skin
  • Easy bruising
  • Dystrophic scars
  • Striae
  • Exotropia
  • Myopia
  • Pneumothorax
  • Hernia
  • Dural ectasia

The vascular phenotype in patients with SMAD3 mutations is very similar to TGFBR1/2 patients.